One dose of gene therapy gives years of relief from blood disorder

Nature, Published online: 17 June 2025; doi:10.1038/d41586-025-01842-1The average number of bleeding episodes for men with haemophilia B dropped almost tenfold after treatment.

Jun 17, 2025 - 19:36
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One dose of gene therapy gives years of relief from blood disorder

Nature, Published online: 17 June 2025; doi:10.1038/d41586-025-01842-1The average number of bleeding episodes for men with haemophilia B dropped almost tenfold after treatment.