In vivo haemopoietic stem cell gene therapy enabled by postnatal trafficking
Nature, Published online: 28 May 2025; doi:10.1038/s41586-025-09070-3In vivo gene delivery to haematopoietic stem and progenitor cells in newborn mice using engineered lentiviral vectors shows promise as an effective treatment for genetic diseases.
Nature, Published online: 28 May 2025; doi:10.1038/s41586-025-09070-3In vivo gene delivery to haematopoietic stem and progenitor cells in newborn mice using engineered lentiviral vectors shows promise as an effective treatment for genetic diseases.
